They Created a Drug for Susannah. What About Millions of Other Patients?
A New York Times feature following Susannah’s journey on how scientists created a bespoke drug to shut down a glitch in the KIF1A gene which affects her nervous system. The KIF1A disorder can present with delays in cognitive and physical development.
The Weinberg Family Cerebral Palsy Center's Pediatric Neurologist Dr. Jennifer Bain administered the medication for Susannah. Read the story on the remarkable results of the treatment.
Read the feature here. Paid subscription is required.